Status | Study |
Recruiting |
Study Name: CD34+ Stem Cell Selection for Patients Receiving Allogeneic Stem Cell Transplantation for Non-Malignant Disease Condition: Bone Marrow Failure Syndrome Severe Aplastic Anemia Severe Date: 2013-10-17 Interventions: Biological: CD34 Stem Cell Selection Therapy The CliniMacs (PLUS) Reagent System (Miltenyi CliniMacs CD3 |
Recruiting |
Study Name: Multi-Center Study of Iron Overload: Survey Study (MCSIO) Condition: Sickle Cell Disease Thalassemia Diamond-Blackfan Anemia Date: 2013-07-30 |
Recruiting |
Study Name: BMT Abatacept for Non-Malignant Diseases Condition: Hurler Syndrome Fanconi Anemia Glanzmann Thrombasthenia Date: 2013-07-24 Interventions: Drug: Abatacept All patients will receive 4 doses of abatacept in addition to standard GVHD prophylaxis |
Recruiting |
Study Name: Bone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders Condition: Chronic Kidney Disease Acute Myeloid Leukemia (AML) Acute Date: 2012-12-17 Interventions: Procedure: Haploidentical Bone Marrow/Kidney Combined bone marrow and kidney transplantation using a hap |
Enrolling by invitation |
Study Name: Unrelated HSCT in Patients With Fanconi Anemia Condition: Fanconi Anemia Date: 2012-10-19 Interventions: Biological: CD34+ selected cells Compassionate treatment of Fanconi Anemia patients with unrelated bone |
Recruiting |
Study Name: Quercetin in Children With Fanconi Anemia; a Pilot Study Condition: Fanconi Anemia Date: 2012-07-25 Interventions: Drug: Quercetin (dietary supplement) Quercetin will be given orally on a twice a day schedule starting w |
Recruiting |
Study Name: Human Placental-Derived Stem Cell Transplantation Condition: Mucopolysaccharidosis I Mucopolysaccharidosis VI Adrenoleu Date: 2012-04-25 Interventions: Drug: Human Placental Derived Stem Cell Infusions of thawed HPDSC to be given following UCB infusion. |
Recruiting |
Study Name: Microcephaly Genetic Deficiency in Neural Progenitors Condition: Microcephaly Date: 2012-02-29 |
Active, not recruiting |
Study Name: Fludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem Cell Transplant in Treating Patients With Hematologic Malignancies Condition: Accelerated Phase Chronic Myelogenous Leukemia Adult Acute Lymphoblastic Leukemia in Remissi Date: 2012-02-06 Interventions: Drug: fludarabine phosphate Gi |
Recruiting |
Study Name: Safety and Efficacy Study of Sotatercept in Adults With Transfusion Dependent Diamond Blackfan Anemia Condition: Diamond Blackfan Anemia Date: 2011-10-31 Interventions: Drug: Sotatercept |